What is Exondys 51?
Exondys 51 is a drug, developed by a company called Sarepta Therapeutics that could slow down the progression of Duchenne muscular dystrophy in patients like O
Haroon, 27, has Facioscapulohumeral muscular dystrophy (FSH) and lives in Lambeth.
Katie Hammond, 30, lives in Hampshire and has facioscapulohumeral muscular dystrophy.
Alison and Ron Barr’s thirteen-year-old son, James, has Duchenne muscular dystrophy and – because he has a mutation amenable to the skipping of exon 51 – he could benefit fro
Laurie Wallis, 55, works as an HR Administrator on the Isle of Wight. She was diagnosed with oculopharyngeal muscular dystrophy (OPMD) in 2003.
At the end of May, Trudi Maples and her friend Rory from Peterborough will be taking on the London to Brighton challenge, 100 kilometres on foot in aid of Muscular Dystrophy UK.
David Morgan, 59, from Eastbourne, trained as a counsellor after being diagnosed with Inclusion Body Myositis in 2005 so that he could help other people with the same condit
Sue Hardman’s nine-year-old son, Charlie, has Duchenne muscular dystrophy and – because he has a mutation amenable to the skipping of exon 51 – he could benefit from new drug
It’s not too late to sign up for our Pedal, Paddle, Peak challenge! Be part of Muscular Dystrophy UK’s successful adventure challenge and pedal, paddle and hike across the
Keira George-Lowe’s six-year-old son, Mitchell, has Duchenne muscular dystrophy and is eligible for new drug, Exondys 51.
Mike Townend, CEO of Rubik’s Cube, is running the London Marathon to raise money for Muscular Dystrophy UK.