Breaking: Update on Translarna NHS treatment for Duchenne muscular dystrophy
The MAA has been extended until January 2023.
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Promising treatment for SMA Type 1 available on the NHS in England
08/03/2021MDUK is delighted to bring you the news that a highly complex, innovative gene therapy is to become available on the NHS in England for the treatment of SMA type 1.
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New £30m fund to install Changing Places toilets in existing buildings across England
04/03/2021Local authorities will soon be invited to ‘opt in’ to receive a proportion of the £30m funding, based on need, to install facilities in existing buildings their communities.
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Four charities call on SMC to approve treatment for Duchenne muscular dystrophy
02/03/2021A group of charities, including Muscular Dystrophy UK, is urging for the approval of a drug that can treat an underlying genetic cause of a life-limiting muscle-wasting condition.
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CHMP gives positive opinion on Evrysdi (risdiplam) for the treatment of SMA
26/02/2021EMA committee gives positive opinion on Evrysdi (risdiplam) for the treatment of SMA
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Muscular Dystrophy UK highlights a master craftsman to mark Rare Disease Day 2021
26/02/2021On this year’s Rare Disease Day, Sunday 28 February 2021, we are showcasing the achievement of master craftsman Paul Tomlin and his amazing, traditional building skills.
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First gene therapy trial for DMD to start recruitment in the UK
25/02/2021For the first time, a clinical trial will start recruiting a small number of boys in the UK to test a potential gene therapy for the treatment of DMD.
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MDUK CEO is taking on the toughest physical challenge of her career
23/02/2021Catherine Woodhead is embarking on a huge challenge of walking the distance between Land’s End and John O’Groats (LeJog)
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In memory of Valerie Patrick, Vice President of MDUK
19/02/2021It is with deep sadness that Muscular Dystrophy UK has learned of the death of Valerie Patrick following a period of ill health.
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Covid-19: MDUK signs open letter calling for Emergency Support Fund
17/02/2021CEO Catherine Woodhead has added her name to an open letter as part of the #RightNow campaign.
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Breaking Covid-19 news: Extra 820,000 vulnerable people in England to be offered vaccine and advised to shield
16/02/2021A new technology called QCovid can analyse a combination of risk factors based on medical records to assess whether somebody may be more vulnerable than was previously understood.