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Read the latest news, browse other people's stories and find blogs about experiences you relate to. You can also read our publications like Target MD, and find our most recent press releases.

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Woman looking through a microscope
We’ve been awarded funds to support researchers in the early stages of their careers
Earlier this year, the Government announced a further £45million to support charity-funded early-…
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Blog
a science lab
Helping us understand congenital myopathies: a new study of changes to an important muscle protein is providing insights
RyR1-related muscle conditions The ability of a muscle to contract, allowing us to move, depends…
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Approval of Duvyzat (givinostat) for Duchenne muscular dystrophy in the USA
The news follows on from Italfarmaco Group announcing results from the EPIDYS clinical trial…
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Blog
Closeup of a lab
The role of periostin in Duchenne muscular dystrophy  
Duchenne muscular dystrophy (DMD) is a condition caused by genetic changes in the dystrophin gene…
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A photo of Professor Linda Popplewell, a research scientist who works on Muscular Dystrophy and rare diseases.
Recognising scientist Linda Popplewell on International Day of Women and Girls in Science
A career in science and muscular dystrophy I’ve always had a brain for science as opposed to…
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News
News update
Understanding your views of vamorolone, a treatment for Duchenne muscular dystrophy currently being appraised by NICE
We are supporting this process as one of two ‘Patient Experts’, and our Director of Care, Campaigns…
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The European Medicines Agency confirms recommendation for non-renewal of authorisation in the EU of Duchenne muscular dystrophy medicine Translarna
In September 2023 we shared news that the European Medicine Agency’s (EMA) human medicines…
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News
Dr Kate Adcock, Professor Laurent Servais, Dame Kay Davies and Professor Matthew Wood
Changing the landscape for clinical trials in the UK - celebrating the fifth anniversary of the MDUK Oxford Neuromuscular Centre
In January 2019, we partnered with the University of Oxford to form the MDUK Oxford Neuromuscular…
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Sarepta Therapeutics announce start of clinical trial for LGMD2E/R4
Limb girdle muscular dystrophy 2E/R4, also known as beta sarcoglyanopathy, is a progressive genetic…
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Blog
Research Update
Research: Successful use of a self-management support programme in neuromuscular specialist centres
Understanding self-management support programmes Self-management support (SMS) is a care programme…
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