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This year, we will be funding 12 exciting research projects, including three three-year project…
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Myotonic dystrophy is a genetic condition that causes progressive muscle weakness and wasting. It…
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As part of Spinal Muscular Atrophy Awareness Month, we split up our past SMA Muscles Matter videos…
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Within Avalglucosidase alfa’s approval process, MDUK took part in a NICE Scoping Workshop in…
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Through our research into better drugs and treatments, and our involvement in the NICE and the SMC…
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We’re delighted to announce that a new treatment for Pompe disease has been recommended for use by…
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We were joined by Neuromuscular Care Advisors Pam Appleton, from St Georges University Hospital,…
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Following the completion of the Phase 2 clinical trial, Fulcrum therapeutics recruited its first…
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On Saturday, 25 June, Italfarmaco Group announced positive data from the completed placebo-…
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What is Duchenne muscular dystrophy?
Duchenne muscular dystrophy is a serious genetic condition…