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The National Institute for Health and Care Excellence’s (NICE) have published draft guidance ‒…
News
On Friday, 22 September, PTC Therapeutics, the company that manufactures Translarna, issued a…
News
Translarna currently has a conditional marketing approval (authorisation) from the EMA, given in…
Blog
Reducing inequalities
Tackling health inequalities is a long-standing aim of both the UK…
Publication
It is only through your help that we are able to fund vital research, and offer care and support to…
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Today NHS England have released new data which shows nearly three in four babies born with Spinal…
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Newborn babies in the UK are currently screened for nine – soon to be ten – rare, but serious,…
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Zolgensma (Onasemnogene abeparvovec) is now recommended as an option for treating presymptomatic…
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We were pleased to hear Rt Hon Jeremy Hunt MP confirm that the Energy Price Guarantee rise has been…
Blog
The Chancellor of the Exchequer, Rt Hon Jeremy Hunt MP, made an Autumn statement in the House of…