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We appreciate that watching this drama may lead to challenging emotions or raise questions or…
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Pompe disease is a chronic, rare, genetic, progressive metabolic disease which results in severe…
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As well as awareness, the week is also designed to help those who don’t necessarily identify as a…
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I first got into volunteering while doing my degree in public relations. It was that classic case…
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Reviewing the impact of myasthenia gravis on caregivers
An important factor in NICE’s decision…
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Researchers often highlight the importance of teamwork. I worked in an academic environment for…
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UPDATE: On 24 May 2023, Roche published an update in which they stated that the FDA's final…
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Anne shared her emotional story with thousands of people when she officially started this year’s…
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We are excited to welcome the thousands of runners joining us at the historic Bidwells Oxford Town…
Your story
When we first learned that Esmae and Grace both had limb-girdle muscular dystrophy, we found the…