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News, blogs and stories

Read the latest news, browse other people's stories and find blogs about experiences you relate to. You can also read our publications like Target MD, and find our most recent press releases.

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Breaking News
Update on the European Medicines Agency recommendation not to renew Translarna marketing authorisation in the European Union
On Friday, 22 September, PTC Therapeutics, the company that manufactures Translarna, issued a…
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News
Breaking News
European Medicines Agency makes recommendation not to renew Translarna marketing authorisation in the European Union
Translarna currently has a conditional marketing approval (authorisation) from the EMA, given in…
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News
On a bright green background words read "We are investing 1.3 million into new research."
We’ve awarded £1.3 million-worth of new research grants
Our new research grants cover a variety of different muscle-wasting conditions, such as ADSSL1…
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Orange graphic with 'BREAKING NEWS' written in lime green
NICE publishes draft guidance on efgartigimod for treating generalised myasthenia gravis
NICE recommendations Although not NICE's final guidance on this medicine, the draft guidance…
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A woman sits on a sofa with a laptop on her lap. She has short brown hair and wears a denim jacket. She smiles at the screen.
Our virtual therapeutic support groups are launching
Being diagnosed with a muscle-wasting condition often means adjusting to a new and unexpected…
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Close up image of a self propelled wheelchair
Latest figures show some people waiting over four months for NHS wheelchairs
There is a target in place for people to be assessed and wheelchairs to be delivered to them within…
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A woman with brown hair sits at her desk, her laptop is open in the background.
NICE starts appraisal process for Duchenne muscular dystrophy treatment vamorolone
On 1 August 2023, the National Institute of Health and Care Excellence (NICE) formally launched its…
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A baby sleeps in its mothers arms.
We welcome new data which shows treatments are working for babies with SMA
Today NHS England have released new data which shows nearly three in four babies born with Spinal…
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yellow and black train in train station
Proposal to close ticket offices in train stations across England could impact disabled people the hardest
How these closures might affect people with muscular dystrophy  These closures could be…
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The focus of the image is Morvenna who is sat in her wheelchair taking part in a inclusive dance class. She is wearing some patterned blue trousers, smiling and waving a ribbon. In the background, there are other people dancing and waving ribbons.
We’re proud to reveal our refreshed brand which will help us to reach and support more of our community
People often think of a brand as a name and logo. But it's about who we are, what we do and why we…
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