Celebrating 20 years: NorthStar a ‘shining light’ for people living with Duchenne muscular dystrophy September 7, 2024 By ellen moye
NICE publishes draft guidance on vamorolone for treating Duchenne muscular dystrophy March 27, 2024 By
NICE starts appraisal process for Duchenne muscular dystrophy treatment vamorolone August 18, 2023 By
Approval of gene therapy SRP-9001 in the USA ‒ a significant milestone in the treatment of Duchenne muscular dystrophy June 23, 2023 By
US FDA advisory committee votes on Sarepta SRP-9001 gene therapy to treat Duchenne muscular dystrophy ahead of a FDA’s final decision May 19, 2023 By
NICE publishes final guidance recommending access to Duchenne muscular dystrophy treatment Translarna January 19, 2023 By
NICE publishes draft guidance on access to Duchenne muscular dystrophy treatment Translarna September 29, 2022 By
10 treatments either available or being appraised in major milestone for the community July 22, 2022 By