These are exciting times, with fresh news about research developments appearing every week.
Find out about the latest research news below and also visit our Breaking News in Research page.
Update on UNITE-DMD gene therapy trial
Work has begun in Professor George Dickson’s lab to refine the gene therapy product.
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CMT gene therapy trial to start in 2019
15/10/2018Sarepta Therapeutics has announced that it will be working with Dr Zarife Sahenk from Nationwide Children’s Hospital in the United States to develop a gene therapy for CMT.
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Update on DMD gene therapy trial
04/10/2018Sarepta Therapeutics has released an update on the four boys dosed in its ongoing gene therapy trial.
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SMA gene therapy trial starts in the UK
01/10/2018We would like to inform you that recruitment for AveXis’ STRIVE-EU gene therapy trial has started at Great Ormond Street Hospital.
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Pain-free and more effective: improving how we monitor SMA
29/09/2018Monitoring the progression of muscle-wasting conditions is essential to ensure they can be managed well.
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Scoping out new treatments for SMA from existing drugs
26/09/2018An old drug could help boost new treatments for people with SMA
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Evaluating a new way to help adults manage their muscle-wasting condition
16/09/2018If you have a progressive condition, finding ways to look after your health to help you stay well is vitally important.
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Meet the families funding a new project to understand LMNA-CMD
13/09/2018Many of the conditions we support at Muscular Dystrophy UK are rare, but few are as rare as LMNA-CMD.
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New insights into muscle fibre loss in Duchenne muscular dystrophy
07/09/2018Professor Jenny Morgan and her team at University College London (UCL) have shown that a type of cell death called necroptosis has an important role in Duchenne muscular dystrophy.
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£1.2m invested in 10 new research projects for 2018
03/09/2018Muscular Dystrophy UK is investing £1.2 million into 10 new research projects this year, bringing our total research portfolio to over £9.7m.
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New study demonstrates the potential of gene editing to treat Duchenne
31/08/2018MDUK-funded researchers in collaboration with others have shown that genome editing can restore dystrophin production in dogs with Duchenne muscular dystrophy.