These are exciting times, with fresh news about research developments appearing every week.
Find out about the latest research news below and also visit our Breaking News in Research page.
NICE to begin appraisal of SMA treatment risdiplam in autumn
NICE will begin its appraisal of the SMA treatment risdiplam this autumn to decide whether or not the treatment will be made available on the NHS in England.
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MDUK Muscles Matter 2020 – Monday 14 September round-up
15/09/2020Our MDUK Muscles Matter 2020 seminars continued on Monday 14 September, virtually bringing together people living with muscle-wasting conditions from across the UK.
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Clinical trial starts for potential Becker muscular dystrophy drug
21/08/2020A clinical trial is under way for EPM-01 – a potential treatment for boys and men with Becker muscular dystrophy that has shown early promise.
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Collagen VI-related myopathies research findings
05/08/2020Muscular Dystrophy UK has provided funding for Professors Muntoni and Bönneman for their project-work relating to collagen VI-related myopathies.
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Muscular Dystrophy UK and Healx announce partnership to identify FSHD treatments
15/07/2020MDUK and Healx announce new partnership to identify FSHD treatments
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AMRC calls on Government to match-fund charity research
25/06/2020AMRC calls on Government to match-fund charity research
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AMRC predicts medical research charities will lose 38 percent of income
12/06/2020A recent survey by the Association of Medical Research Charities (AMRC) has found that members – including Muscular Dystrophy UK – will experience an average loss of 38 percen
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Roche extends Risdiplam compassionate use programme
11/06/2020Roche, the pharmaceutical company behind the SMA treatment Risdiplam, has extended its compassionate use programme to potentially include patients who cannot receive Spinraza becau
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Request for NICE to reconsider the decision to suspend the appraisal process for risdiplam
07/05/2020Joint letter to NICE regarding the suspension of the appraisal process for ridisplam