These are exciting times, with fresh news about research developments appearing every week.
Find out about the latest research news below and also visit our Breaking News in Research page.
AMO Pharma announces clinical trial for AMO-02 in the treatment of Congenital Myotonic Dystrophy
AMO-Pharma announces the initiation of Phase 2/3 clinical trial, REACH-CDM.
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Important announcement for adults with Duchenne muscular dystrophy
18/12/2020Muscular Dystrophy UK is delighted to announce the successful completion of two projects we funded to improve care and support for adults living with Duchenne muscular dystrophy.
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Update on stoppage of SIDEROS clinical trial for Raxone/idebenone
18/12/2020Update on stoppage of SIDEROS clinical trial for Raxone/idebenone
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PepGen secures $45m investment to drive molecular patches to clinic
10/12/2020PepGen’s work into molecular patches seeks to help people with Duchenne muscular dystrophy (DMD) and other muscle-wasting conditions.
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Green light for a Duchenne muscular dystrophy gene therapy in France
07/12/2020These are exciting times for the development of treatments, some of which have the potential to markedly improve outcomes for a number of neuromuscular conditions.
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SMC approves mexiletine hydrochloride for adults with non-dystrophic myotonic disorders
07/12/2020The news means adult patients in Scotland will be able to access mexiletine hydrochloride on the NHS if their healthcare professional thinks it is right for them.
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Cambridge University Hospitals’ Trust decision on risdiplam
04/12/2020Cambridge University Hospitals’ Trust decision on risdiplam
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SMA research project update- The potential of an existing drug to treat SMA
01/12/2020Dr Melissa Bowerman is investigating whether a commercially available drug that targets the body’s metabolism could be a potential treatment for SMA.
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Looking at microdystrophin in the heart
11/11/2020Dr Federica Montanaro, at the UCL Great Ormond Street Institute of Child Health, is leading an important piece of research into heart disease in Duchenne and Becker MD.
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MDUK Muscles Matter 2020 – Saturday 10 October round-up
10/10/2020MDUK Muscles Matter 2020 – Saturday 10 October round-up