Where would we be without funding from Muscular Dystrophy UK? The basic answer is we wouldn’t be anywhere.

Professor Doug Turnbull, Professor of Neurology at the University of Newcastle.

There are currently no treatments for most of the muscle-wasting conditions we support. Research generates the knowledge that is essential for understanding the cause of these conditions. This knowledge can then be used in finding effective treatments.

Since 1959 we have invested more than £55 million in high quality research into muscle-wasting conditions. This has been possible only through the generosity and dedication of our supporters.

We use a robust international peer-review system, and have laid the foundations for the first potential treatments for some muscle-wasting conditions.

We have contributed to crucial scientific breakthroughs:

• laying the foundations for the promising technology of ‘exon skipping’ which is currently being tested in clinical trials for boys with Duchenne muscular dystrophy
• funding work that has led to a scientific breakthrough in finding a treatment for mitochondrial myopathy, now close to clinical trial.

We are also pressing to ensure early participation for UK patients in clinical trials. We fund clinical trial co-ordinators and the national neuromuscular database to ensure vital patient information is available to clinicians and researchers.

We won’t stop until there are treatments and cures for all muscle-wasting conditions. We cannot do this without your support – please help us now.


  • Professor Robin Lovell-Badge

    Genome editing media briefing

    A panel of scientists answered the journalists questions

    Read more »

  • pills

    New Drug Application for eteplirsen

    The exon skipping drug could be approved by 2016 in the US

    Read more »

  • chalk-board

    Children and clinical research

    Nuffield Council on Bioethics' report

    Read more »

  • blue pills

    Rimeporide receives Orphan Drug Designation

    The news was announced by EspeRare

    Read more »

Events calendar

  • 29

    Question of Support Dinner & Quiz

    29 May 2015

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  • 30

    Edinburgh Marathon Festival – Day One

    30 May 2015

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  • 30

    Glasgow Central Station Collection

    30 May 2015

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