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Josie is a fun loving, artistic five-year-old who loves school, swimming, playing with her little…
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Emery-Dreifuss muscular dystrophy (EDMD) affects approximately one in every 250,000 people. EDMD is…
Your story
I’ve always been very active – I think that’s why being in the Fire Brigade suited me so well.
I…
Your story
When I was diagnosed with myositis – a rare auto-immune disorder that involves chronic inflammation…
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On January 9th 2023, following a small number of children having suspected significant adverse drug…
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Zolgensma (Onasemnogene abeparvovec) is now recommended as an option for treating presymptomatic…
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We were pleased to hear Rt Hon Jeremy Hunt MP confirm that the Energy Price Guarantee rise has been…
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Why are you fundraising for MDUK?
I’ve attended MDUK’s Celebrity Sports Quiz events at Lords…
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Many people would have been shocked and surprised by such a negative and inaccurate worldview being…
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What is spinal muscular atrophy?
Spinal muscular atrophy (SMA) is a rare muscle-wasting condition…