Where would we be without funding from Muscular Dystrophy UK? The basic answer is we wouldn’t be anywhere.
Professor Doug Turnbull, Professor of Neurology at the University of Newcastle.
There are currently no treatments for most of the muscle-wasting conditions we support. Research generates the knowledge that is essential for understanding the cause of these conditions. This knowledge can then be used in finding effective treatments.
Since 1959 we have invested more than £55 million in high quality research into muscle-wasting conditions. This has been possible only through the generosity and dedication of our supporters.
We use a robust international peer-review system, and have laid the foundations for the first potential treatments for some muscle-wasting conditions.
We are also pressing to ensure early participation for UK patients in clinical trials. We fund clinical trial co-ordinators and the national neuromuscular database to ensure vital patient information is available to clinicians and researchers.
We won’t stop until there are treatments and cures for all muscle-wasting conditions. We cannot do this without your support – please help us now.
Joint letter to NICE regarding ridisplam
Join us for our Virtual Celebrity Sports Quiz
NICE, NHS England and NHS Improvement have taken advice
The SMA gene therapy Zolgensma has today been grant