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1. SMA is a progressive muscle wasting condition  Over time, SMA causes muscle weakness and loss…
Blog
Earlier this year, a team led by researchers at Newcastle University conducted a study to shed…
News
MDUK will call for improved multidisciplinary care across Scotland at the Cross-Party Parliamentary…
News
We were delighted to be joined in our SMA seminar by SMA researchers Dr Melissa Bowerman and Sam…
News
Risdiplam is an oral drug that increases SMN protein levels by targeting the SMN2 gene manufactured…
News
In early December, Muscular Dystrophy UK and SMA UK reported our disappointment that, despite the…
News
Muscular Dystrophy UK and SMA UK were extremely disappointed to learn earlier this week that,…
News
Recent advances in SMA research have led to the exciting development of genetic therapies, such as…
News
We are pleased to announce that the 2017 Spinal Muscular Atrophy (SMA) best practice care guide for…
News
NICE widens scope of its appraisal of Zolgensma This will now be in line with the European…