Update on UNITE-DMD gene therapy trial
Work has begun in Professor George Dickson’s lab to refine the gene therapy product.
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CMT gene therapy trial to start in 2019
15/10/2018Sarepta Therapeutics has announced that it will be working with Dr Zarife Sahenk from Nationwide Children’s Hospital in the United States to develop a gene therapy for CMT.
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Trailblazers attend Loughborough University Hackathon
15/10/2018On September 27th Trailblazers attended the Global Disability Innovation Hub event “Hacking Disability – How do you change a lightbulb if you use a wheelchair?” Loughborough U
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Countdown to the MDUK Championship Powerchair Football season
11/10/2018MDUK Championship Powerchair Football starts Saturday
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UK Independent Mechanism updates UN on Disabled Peoples Rights
11/10/2018The United Nations Committee on the Rights of Persons with Disabilities held a review into the state of accessibility and inclusion in 2017, and this report updates the committee.
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Gabby Logan appointed new President of Muscular Dystrophy UK
10/10/2018British presenter and former Welsh international gymnast Gabby Logan is to be the new President of Muscular Dystrophy UK.
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New ultra-orphan pathway in Scotland
08/10/2018The Scottish Government have announced details about a new ultra-orphan pathway
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Becker Awareness Week 2018
07/10/2018Becker Awareness Week 2018 runs from 7 October to 13 October, and is a chance for us all to show our support and help people understand the condition.
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Update on DMD gene therapy trial
04/10/2018Sarepta Therapeutics has released an update on the four boys dosed in its ongoing gene therapy trial.
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MDUK Scottish Premiership & Championship Preview
03/10/2018Scottish Powerchair Football begins soon
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SMA gene therapy trial starts in the UK
01/10/2018We would like to inform you that recruitment for AveXis’ STRIVE-EU gene therapy trial has started at Great Ormond Street Hospital.