Our Royal Patron, The Duke of Edinburgh, has died
Prince Philip, Royal Patron of Muscular Dystrophy UK, has died.
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Highlights of the 2021 Neuromuscular Translational Research Conference
08/04/2021The conference brought together scientists and clinicians from around the world to share the latest advances in cutting-edge research.
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Have your say on where to install Changing Places toilets in England
08/04/2021Add your voice to our biggest consultation yet
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NICE statement on Translarna
06/04/2021Muscular Dystrophy UK and Action Duchenne have received a public statement from NICE on ataluren (Translarna).
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SMA drug Evrysdi (risdiplam) approved in the EU
30/03/2021The European Commission (EC) has granted marketing authorisation to Evrysdi™ (risdiplam) for the treatment of spinal muscular atrophy (SMA).
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Join William Sitwell and Jesse Dunford Wood for cooking and wine event
29/03/2021William Sitwell and Jesse Dunford Wood – both regular Masterchef critics – will share insider tips during an evening of entertainment between 7pm-8.30pm on April 29.
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Updates from the FSHD, myotonic dystrophy, Col6- dystrophies and GNE myopathy registries
26/03/2021The patient registries for FSHD, DM, COL6-dystrophies and GNE myopathy have shared their latest newsletters.
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Pharnext shares update on its clinical development of CMT1A drug
24/03/2021The pharmaceutical company Pharnext is on track to start its phase III clinical trial, PREMIER in the USA, by the end of March 2021.
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Muscular Dystrophy UK launches 2021 research grant round
09/03/2021Muscular Dystrophy UK is delighted to announce the launch of its 2021 grant round.
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SMA gene treatment Zolgensma accepted for restricted use within NHS Scotland
08/03/2021SMA gene treatment Zolgensma accepted for restricted use within NHS Scotland
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Promising treatment for SMA Type 1 available on the NHS in England
08/03/2021MDUK is delighted to bring you the news that a highly complex, innovative gene therapy is to become available on the NHS in England for the treatment of SMA type 1.