Stephanie Castelete-Tyrrell has congenital muscular dystrophy and says gaming gives her the freedom to “complete tasks that many people take for granted in the real world".Read more
MDUK Muscles Matter 2020 – Wednesday 9 September round-up
The REAL Wonder Woman actress has thrown her support behind Carmela’s 2,000 kilometre walk in search of her favourite superhero.10/09/2020
Gal Gadot, the REAL Wonder Woman actress has thrown her support behind Carmela’s 2,000 kilometre walk in search of her favourite superhero.
Trailblazers network moves over to charity Whizz-Kidz
Free online physiotherapy sessions for people with muscle-wasting conditions
NICE widens scope of its appraisal of Zolgensma TM
MDUK Muscles Matter 2020 – Tuesday 25 August round-up
A clinical trial is under way for EPM-01 – a potential treatment for boys and men with Becker muscular dystrophy that has shown early promise.
On Monday 17 August, Roche announced that the European Medicines Agency (EMA) has validated the Marketing Authorization Application (MAA) for risdiplam for patients with SMA.
The oral spinal muscular atrophy (SMA) drug Risdiplam has been approved by the FDA (U.S. Food and Drug Administration).
Muscular Dystrophy UK has provided funding for Professors Muntoni and Bönneman for their project-work relating to collagen VI-related myopathies.