Tributes paid to determined twins
Loving tributes have been paid to the determination of twin brothers in North East Derbyshire who lived with Becker MD and who have died within 12 months of one another.
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Spinraza set to be available for NHS use for patients with SMA Types 1, 2 and 3
15/05/2019The SMA treatment Spinraza is set to be available on the NHS in England
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Government launches Changing Places consultation
13/05/2019The government has launched a public consultation into making Changing Places toilets mandatory in new, large public buildings, following years of hard work by campaigners.
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Employability report launched at Parliament
10/05/2019On Wednesday 8th May, Trailblazers held a Reception at the House of Commons hosted by Heidi Allen MP to launch the new ‘Ready and Able’ report.
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Tireless Tyrone fundraiser is awarded an MBE
09/05/2019Tireless Tyrone fundraiser for Muscular Dystrophy UK, Claire O’Hanlon visited to Buckingham Palace to receive an MBE.
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New MDUK-funded study investigating genetic tools to correct Collagen VI mutation
09/05/2019MDUK-funded researchers have corrected a common mutation causing Ullrich congenital muscular dystrophy in the laboratory.
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Sarepta acquires rights to sixth LGMD gene therapy
08/05/2019Sarepta Therapeutics announced today that it has signed an agreement with Nationwide Children’s Hospital (Ohio, USA) to develop a gene therapy for LGMD type 2A.
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Trailblazers’ ‘Ready and able’ report highlights changes needed for disabled job-seekers
08/05/2019Muscular Dystrophy UK is calling on the government and employers to take action to remove the barriers that make it difficult for disabled people to find and stay in work.
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Care recommendations for congenital myotonic dystrophy and myotonic dystrophy type 2 published
03/05/2019The first set of care recommendations for congenital and childhood-onset myotonic dystrophy type 1, and myotonic dystrophy type 2 have been published.
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Trailblazers launch survey into disabled women’s access to healthcare
02/05/2019Find out more about Trailblazers' new investigation.
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Muscular Dystrophy UK and Spinal Muscular Atrophy UK call for urgent action on Spinraza
02/05/2019Act now or babies will needlessly die – that is the message from Muscular Dystrophy UK and Spinal Muscular Atrophy UK ahead of a fourth NICE committee meeting next week about Spi