Latest news on access to Spinraza
Along with other patient groups and clinicians we have written to NICE and NHS England about access to Spinraza.
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Eminent professor’s son completes half marathon in his father’s name
10/04/2019Eminent professor, Professor Alan Eglin Heathcote Emery spent his professional life researching muscular dystrophy.
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Georgia is running the London marathon for boyfriend James
09/04/2019"This has made us appreciate the life we have together. In the past two years we've been some amazing places. That is not about to stop."
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Audentes starts therapy development for DMD and myotonic dystrophy
08/04/2019Audentes Therapeutics has announced that it will begin the development of new genetic medicines for Duchenne muscular dystrophy and myotonic dystrophy type 1.
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Hannah’s Royal Parks Half For Simon
04/04/2019Hannah Mcfarland ran the Royal Parks Half Marathon for Muscular Dystrophy UK last year using one of our golden bond spaces.
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Charity Partnership with Belfast-based Portview raises £32,000!
04/04/2019Generous employees of leading fit-out specialist, Portview, have raised more than £32,000 for Muscular Dystrophy UK to fund vital research into muscle-wasting conditions.
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Results from gene therapy trial for limb girdle muscular dystrophy type 2D
02/04/2019One adult and six children with LGMD2D were treated with the gene therapy MYO-102. The treatment was safely delivered to their muscles and a new clinical trial is being planned.
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Sarepta announces positive preliminary results from DMD trial
29/03/2019Sarepta Therapeutics has released positive preliminary results from one of its clinical trials testing exon skipping in Duchenne muscular dystrophy.
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Santhera prepares to request approval for idebenone in DMD
28/03/2019Santhera Pharmaceuticals has provided an update on its plans to request approval for Puldysa in Duchenne muscular dystrophy.
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Seven new centres awarded Centres of Clinical Excellence status
27/03/2019Seven new centres that support people with muscle-wasting conditions have been awarded Centres of Clinical Excellence status by Muscular Dystrophy UK, taking the total across the U