A pilot study to establish a new tool to investigate motor skills in SMA mouse models
Assessing a non-invasive approach to detect myopathy in children
Identification of Charcot-Marie-Tooth disease therapies through drug repurposing
New concepts for the treatment of mitochondrial myopathies
Developing advanced molecular patch therapy for collagen VI-related congenital muscular dystrophy
Understanding the impact of additional genes in animal models of LAMA2-related dystrophies
Improving muscle function by reducing scaring and restoring dystrophin in Duchenne muscular dystrophy